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IJMS | Free Full-Text | Nusinersen Modulates Proteomics Profiles of Cerebrospinal Fluid in Spinal Muscular Atrophy Type 1 Patients
Antisense oligonucleotides (ASOs) in clinical use. (A) Nusinersen binds... | Download Scientific Diagram
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Nusinersen (Spinraza®) – Spinal Muscular Atrophy (SMA) | National Institute of Neurological Disorders and Stroke
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